News & Events

Photo of a sleeping baby in relation to Kids Research Spinal Muscular Atrophy trials and success
Webinar series
Advanced Therapeutics: No longer science fiction – a look at how gene therapy is changing the game for children with SMA In our upcoming webinar, we will be visiting the topics of newborn bloodspot screen and genetic therapies in the context of treating Spinal Muscular Atrophy (SMA). We will hear from a panel of speakers who will discuss our centres success in establishing a multidisciplinary...
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Webinar series
In the 7th instalment of our Advanced Therapeutics Webinar series we focused on ethical considerations in rare disease clinical trials. As new treatments become available, and in populations without prior access, concerns around equity and suitability arise. Physicians, patients and their families can be faced with a situation where there are more patients than clinical trial spots. So, who...
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Webinar series
Our Advanced Therapeutics Webinar has returned in 2022 with "Who you gonna call? Drug busters!". In this 6th episode of the series we focused on pharmacy considerations for working with Advanced Therapeutics. Hosted by Acting Director of Research, Dr Paula Bray and Advanced Therapeutics Medical Lead at Sydney Children’s Hospital, Randwick, Dr Laura Fawcett, we heard from three senior phar...
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