News & Events

Two young sisters with a blinding eye condition will now have access to ocular gene therapy after a new pathway to the treatment was discovered. The girls, who were diagnosed with early-onset severe retinal dystrophy (EOSRD), an inherited degenerative disease of the retina, began having trouble with their night vision at four and two years of age. With few effective treatments available for...

The Sydney Children’s Hospitals Network (SCHN) and Children’s Medical Research Institute (CMRI) are pleased to announce the establishment of the Australian Genome Therapeutics Centre (AGTC), which will transform the treatment of children with serious inherited diseases and contribute to the development of exciting new treatment options for a wide range of other diseases, including cancer, across...

International Clinical Trials Day is celebrated around the world in May to acknowledge and celebrate the many people who are involved in clinical trials. It is also a unique opportunity to raise awareness about the importance of clinical trials and clinical research as a career option – among the greater public. Learn more about Clinical Trials Day here Read the words written by Aimee Williams...

Registration now open! Register now and join our 3rd webinar of the Advanced Therapeutics series. In this webinar, we will be focusing on Ocular Gene Therapy, the first in vivo gene therapy approved by the Therapeutic Goods Administration (TGA) here in Australia for clinical use in inherited retinal diseases. Inherited retinal diseases are a group of conditions that disproportionately affect c...