News & Events

  • 16 August 2021
Gene Therapy
New research has shown that gene therapy may provide an effective treatment for Spinal Muscular Atrophy (SMA), a devastating and fatal genetic condition. The first part of the results from the SPR1NT trial were presented at the European Academy of Neurology (EAN) Conference recently.  What is SMA? SMA affects the motor nerve cells in the spinal cord, causing progressive muscle weakness...
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Gene Therapy
The Sydney Children’s Hospitals Network (SCHN) and Children’s Medical Research Institute (CMRI) are pleased to announce the establishment of the Australian Genome Therapeutics Centre (AGTC), which will transform the treatment of children with serious inherited diseases and contribute to the development of exciting new treatment options for a wide range of other diseases, including cancer, across...
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gene therapy
A gene therapy project to save infants’ lives has been named the top-ranked National Health and Medical Research Council (NHMRC) Ideas Grant for 2020. The project led by Professor Ian Alexander and his team were awarded the 2020 NHMRC Marshall and Warren Ideas Grant Award at the NHMRC Research Excellence Awards Dinner on June 16th. Professor Ian Alexander, Head of the Gene Therapy Research Uni...
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  • 19 May 2021
Clinical Trials
International Clinical Trials Day is celebrated around the world in May to acknowledge and celebrate the many people who are involved in clinical trials. It is also a unique opportunity to raise awareness about the importance of clinical trials and clinical research as a career option – among the greater public. Learn more about Clinical Trials Day here Read the words written by Aimee Williams...
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  • 05 May 2021
Webinar Series
Watch the video of this webinar to hear from two experts in the fields of genetic retinal diseases and stem cell biology discuss Ocular Gene and Cell Therapies and the tremendous new hope they bring to the treatment of these retinal diseases. Ocular Gene Therapy is the first in vivo gene therapy approved by the Therapeutic Goods Administration (TGA) here in Australia for clinical use...
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  • 01 April 2021
Webinar Series
Registration now open! Register now and join our 3rd webinar of the Advanced Therapeutics series. In this webinar, we will be focusing on Ocular Gene Therapy, the first in vivo gene therapy approved by the Therapeutic Goods Administration (TGA) here in Australia for clinical use in inherited retinal diseases. Inherited retinal diseases are a group of conditions that disproportionately affect c...
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  • 25 March 2021
Epilepsy
World Purple Day is celebrated on the 26th March, a day aimed at raising awareness of epilepsy. What is Epilepsy? Epilepsy is one of the most common neurological disorder that affects the brain, often causing seizures. Around 65 million people in the world have epilepsy and although epilepsy can develop at any stage of life, it is more common in children, adolescents and people over 60....
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  • 08 March 2021
Webinar Series
Missed out on our first webinar of the year? Watch the video of this webinar to hear from two esteemed leaders in the field of paediatric cancer and pioneers in CAR-T cell therapy. Chimeric Antigen Receptor (CAR) T cell therapy is the most therapeutic advancement in acute lymphoblastic leukaemia for generations and is a new form of immunotherapy approach to cancer. The CAR-T cell therapy appro...
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  • 24 February 2021
Rare Diseases
Background The 28 of February is International Rare Disease Day, an opportunity to raise awareness around rare diseases and improve access to treatment and medical representation for individuals with rare diseases and their families. There are over 300 million people living with one or more of over 6000 identified rare diseases around the world. Although individually uncommon, there ar...
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  • 09 February 2021
Webinar Series
We are back with our series of webinars which explores the way Advanced Therapeutics is driving clinicians and researchers to prepare for a new wave of therapies, revolutionising the future of paediatric health care. Register now and hear from two esteemed leaders in the field of paediatric cancer and pioneers in CAR-T cell therapy. Chimeric Antigen Receptor (CAR) T cell therapy is the most th...
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