News & Events

Kids Research welcomes the NSW government’s funding boost for biomedical research, putting the state at the forefront of cutting-edge health treatments. The Perrottet government has secured $270 million, announced in the state budget, to go towards two new facilities; the Viral Vector manufacturing facility at Westmead and the Sydney Biomedical Accelerator Complex in Camperdown. Premier Domini...

Babies diagnosed with Spinal Muscular Atrophy (SMA) at birth who received life-changing gene therapy are now celebrating their first birthday symptom-free or with minimal symptoms thanks to Sydney Children’s Hospitals Network’s (SCHN) world-first clinical trial. The SPR1NT trial, published in the prestigious journal Nature Medicine (two copies of SMN2 and three copies of SMN2), successfull...

Wendy Gold is an Associate Professor at the University of Sydney in the School of Medical Sciences, Faculty of Medicine and Health and a Neurobiologist based in the Kids Neuroscience Centre, Kids Research at The Children’s Hospital at Westmead. She teaches third year Medical Science students on the subject of translating medical discoveries into the clinic and leads a research team who...

The benefits of a new precision medicine initiative, being piloted at Sydney Children’s Hospitals Network (SCHN), are already being seen in children and families with rare genetic diseases. The program, Gene2Care, aims to improve the standard of care, including enhanced diagnoses and access to management and treatment. The family-centred program, funded by Luminesce Alliance, combines the effo...