News & Events

Photo of a sleeping baby in relation to Kids Research Spinal Muscular Atrophy trials and success
Webinar series
Advanced Therapeutics: No longer science fiction – a look at how gene therapy is changing the game for children with SMA In our upcoming webinar, we will be visiting the topics of newborn bloodspot screen and genetic therapies in the context of treating Spinal Muscular Atrophy (SMA). We will hear from a panel of speakers who will discuss our centres success in establishing a multidisciplinary...
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Webinar series
In the 7th instalment of our Advanced Therapeutics Webinar series we focused on ethical considerations in rare disease clinical trials. As new treatments become available, and in populations without prior access, concerns around equity and suitability arise. Physicians, patients and their families can be faced with a situation where there are more patients than clinical trial spots. So, who...
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Clinical Trials Day
There has been a dramatic rise in the number of children diagnosed with food allergies over the last two decades, with three in 10 children now developing a food-related allergy or eczema. Food Technology teacher Jessica Bales has witnessed this increase firsthand and says despite taking every precaution, the possible risk factor to the safety of her students induces stress and anxiety. “...
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Webinar series
Our Advanced Therapeutics Webinar has returned in 2022 with "Who you gonna call? Drug busters!". In this 6th episode of the series we focused on pharmacy considerations for working with Advanced Therapeutics. Hosted by Acting Director of Research, Dr Paula Bray and Advanced Therapeutics Medical Lead at Sydney Children’s Hospital, Randwick, Dr Laura Fawcett, we heard from three senior phar...
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International Women's Day
Dr Michelle Lorentzos is a paediatric neurologist, meaning she looks after children who have conditions affecting their brain, nerves or muscles. She has a particular interest in finding treatments for Duchenne muscular dystrophy, a progressive and life-limiting neuromuscular disease affecting boys in childhood.   She also works in the very exciting...
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Grant Success
Earlier this year, several researchers from Kids Research, and our partners at the University of Sydney and UNSW, were awarded National Health and Medical Research Council (NHMRC) funding for their projects, which are focusing on a range of childhood diseases. The five-year Investigator Grants are helping further research in areas including rare genetic disorders and childhood and adolescent o...
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Webinar Series
Watch the video of this webinar to hear from two experts in important parts of the drug development pipeline. So far, our series of webinars has featured a number of therapies currently being delivered to patients at the Sydney Children’s Hospitals Network (SCHN). So we’ve asked the experts how potential therapies are identified and how do we most effectively investigate the effectiveness and saf...
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  • 19 May 2021
Clinical Trials
International Clinical Trials Day is celebrated around the world in May to acknowledge and celebrate the many people who are involved in clinical trials. It is also a unique opportunity to raise awareness about the importance of clinical trials and clinical research as a career option – among the greater public. Learn more about Clinical Trials Day here Read the words written by Aimee Williams...
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  • 24 February 2021
Rare Diseases
Background The 28 of February is International Rare Disease Day, an opportunity to raise awareness around rare diseases and improve access to treatment and medical representation for individuals with rare diseases and their families. There are over 300 million people living with one or more of over 6000 identified rare diseases around the world. Although individually uncommon, there ar...
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  • 09 February 2021
Webinar Series
We are back with our series of webinars which explores the way Advanced Therapeutics is driving clinicians and researchers to prepare for a new wave of therapies, revolutionising the future of paediatric health care. Register now and hear from two esteemed leaders in the field of paediatric cancer and pioneers in CAR-T cell therapy. Chimeric Antigen Receptor (CAR) T cell therapy is the most th...
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